[{"data":1,"prerenderedAt":-1},["ShallowReactive",2],{"condition:pitt-hopkins-syndrome":3},{"name":4,"total":5,"recruiting":6,"trials":7,"biomarkers":29,"states":30},"Pitt-Hopkins Syndrome",3,2,[8,16,22],{"nct_id":9,"title":10,"phases":11,"status":13,"updated_at":14,"content_modified":15},"NCT07135050","Phase 1\u002F2 Study of MZ-1866, an AAV-9 Gene Therapy Delivered by Intracerebroventricular Injection to Participants With Pitt Hopkins Syndrome",[12],"Phase 1\u002FPhase 2","RECRUITING","2026-08-26T02:18:21.216897Z","2026-05-05T02:43:27.964285Z",{"nct_id":17,"title":18,"phases":19,"status":13,"updated_at":20,"content_modified":21},"NCT01793168","Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford",[],"2026-08-26T02:17:29.353236Z","2026-05-13T02:55:06.077983Z",{"nct_id":23,"title":24,"phases":25,"status":26,"updated_at":27,"content_modified":28},"NCT03655223","Early Check: Expanded Screening in Newborns",[],"ACTIVE_NOT_RECRUITING","2026-08-03T03:53:57.297126Z","2026-06-16T05:54:07.977837Z",[],[]]