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Effectiveness",[],"2026-08-26T02:16:29.226604Z","2026-05-05T02:43:27.060371Z",{"nct_id":44,"title":45,"phases":46,"status":13,"updated_at":47,"content_modified":48},"NCT05861999","A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy",[20],"2026-08-26T02:18:13.438956Z","2026-05-05T02:43:27.055234Z",{"nct_id":50,"title":51,"phases":52,"status":13,"updated_at":53,"content_modified":54},"NCT07221669","A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)",[34],"2026-08-26T02:17:56.243868Z","2026-05-05T02:43:26.922524Z",{"nct_id":56,"title":57,"phases":58,"status":13,"updated_at":59,"content_modified":60},"NCT07047144","A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular 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Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies",[],"2026-08-26T02:15:30.699880Z","2026-07-19T19:36:05.036371Z",{"nct_id":86,"title":87,"phases":88,"status":13,"updated_at":89,"content_modified":90},"NCT06955897","Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA",[],"2026-08-26T02:18:25.327036Z","2026-07-05T05:32:16.706774Z",{"nct_id":92,"title":93,"phases":94,"status":13,"updated_at":95,"content_modified":96},"NCT07400198","Gait and Bone Health in SMA",[],"2026-08-26T02:19:01.741747Z","2026-05-13T02:55:06.700520Z",{"nct_id":98,"title":99,"phases":100,"status":13,"updated_at":101,"content_modified":102},"NCT07223489","Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System",[],"2026-08-26T02:18:20.384845Z","2026-05-13T02:55:06.676006Z",{"nct_id":104,"title":105,"phases":106,"status":13,"updated_at":107,"content_modified":108},"NCT06839469","Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders",[],"2026-08-26T02:15:37.042762Z","2026-05-13T02:55:06.583259Z",{"nct_id":110,"title":111,"phases":112,"status":13,"updated_at":113,"content_modified":114},"NCT06194539","Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)",[],"2026-08-03T03:15:35.967581Z","2026-05-13T02:55:06.423429Z",{"nct_id":116,"title":117,"phases":118,"status":13,"updated_at":119,"content_modified":120},"NCT05789758","A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their 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