Fabry Disease clinical trials
13 active trials name this condition. Describe your situation to see which ones you may be eligible for.
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- A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease
- A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- A proof-of Concept Study to Assess Safety and Tolerability of HM15421/GC1134A in Patients With Fabry Disease
- Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- Maternal and Postnatal Outcomes Study (MOS): A Global Observational Registry Assessing the Safety of Elfabrio® in Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- A Study of Patients With Fabry Disease (US Specific)
- A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients
- A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Natural History and Structural Functional Relationships in Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal Disease Study
- Fabry Disease Registry & Pregnancy Sub-registry
- Cardiovascular Multimodality Imaging Study
- Long-Term Follow-up of Subjects Who Were Treated With ST-920
- ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Guides for people searching for a trial
- Why people get turned down — and what to do nextWhat eligibility criteria are for, what keeps people out, and where to go when the first door closes.
- How your biomarkers decide which trials you qualify forEGFR, HER2, BRAF, PD-L1 and the rest — what they are and why they increasingly gate access.
- How to search for a trial without losing your mindWhere to look, what to gather first, and how to read what you find.
- What Phase 1, 2 and 3 actually mean for youWhat each phase is testing, and how to weigh an early-phase trial against a later one.
- 10 questions to ask before you say yesTreatment, time, cost, safety and your rights. Worth bringing to a screening visit.
- You matched with a trial. What happens now?Phone screens, the screening visit, informed consent, and day one.
Showing active trials that list “Fabry Disease” as a condition. Eligibility shown on each trial is an estimate — the trial's study team makes the final decision.