Myotonic Dystrophy Family Registry

This is an online registry called the Myotonic Dystrophy Family Registry (MDFR). It's not testing a new medicine, but rather collecting information from people with Myotonic Dystrophy (DM) to help researchers understand the condition better and find participants for future studies. You can join if you have a confirmed diagnosis of congenital, juvenile-onset, or adult-onset Myotonic Dystrophy type 1 (DM1) or type 2 (DM2). The goal is to gather patient-reported information over 36 months to help develop more effective treatments and improve care for people with DM.

Study design
This is an observational study, meaning it collects information without testing a specific treatment. It aims to include 3500 participants.
What's involved
You would enter your health information into an online database.
Compensation
Not stated in the trial record.
Follow-up
Patient-reported outcomes will be measured for 36 months.

AI-generated from the public study record. Only the study team can confirm whether you're eligible — confirm details with them before making decisions.

NCT02398786

Myotonic Dystrophy Family Registry

Recruiting
Not specifiedAll AgesObservational
Myotonic Dystrophy Foundation
~3,500 participants
Updated 2024-11-21 on ClinicalTrials.gov
What's tested:Patient-entered data

At a glance

Recruiting sites
1 of 1 listed site is recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Patient reported outcomes
Measured over 36 months
Myotonic Dystrophy
Congenital Myotonic Dystrophy
Myotonic Dystrophy 1
Myotonic Dystrophy 2
Dystrophia Myotonica
Dystrophia Myotonica 1
Dystrophia Myotonica 2
Myotonia Dystrophica
Myotonic Dystrophy, Congenital
Myotonic Myopathy, Proximal
PROMM (Proximal Myotonic Myopathy)
Proximal Myotonic Myopathy
Steinert Disease
Steinert Myotonic Dystrophy
Steinert's Disease
Myotonia Atrophica
1 sites across 1 states
California1
  • Tanya Stevenson, EdD, MPH · STUDY_CHAIR · Myotonic Dystrophy Foundation

Opens a ready-to-send draft in your own email app — review before sending.

Do you actually qualify for this trial?

Add a private profile and we'll compare every criterion below against your situation — and tell you which ones are met, uncertain, or excluding.

Check eligibility for this trial ~2 min · HIPAA-protected · delete anytime
Eligibility criteria

Inclusion

Diagnosed with congenital, juvenile-onset or adult onset DM1 or DM2 (confirmed by clinical exam or genetic test)

Exclusion

Not diagnosed with DM, unaffected family members
  • Patient reported outcomes36 months

    Number of patients reporting specific symptoms and symptom severity, as well as impacts to quality of life and overall burden of disease in order to inform clinical trial development, understanding of disease for academic, industry and federal agency stakeholders and overall policy decisions. Results will be analyzed in comparison to other registry data and surveys to characterize this disease population cohort and to further define the population.