Leucovorin for Social and Language Deficits in Young Children with Autism

This study is looking at how a liquid medicine called Levoleucovorin Calcium might help young children with Autism Spectrum Disorder (ASD) improve their social communication. Researchers want to see if this medicine can make a difference in social skills and other symptoms of ASD. You might be able to join if your child is between 2.5 and 5 years old, has an ASD diagnosis, and also has language delays. A special blood test for "Folate Receptor Alpha Autoantibody Positive status" is also required. The study will compare Levoleucovorin Calcium to a placebo (an inactive substance) and will follow participants for about 26 weeks to see if there are improvements in social communication symptoms.

Study design
This study is an interventional trial, meaning participants will receive either the study drug or a placebo. It plans to enroll 80 children across two locations.
What's involved
Participation will last approximately 26 weeks, from the initial screening visit to the end of treatment. You will have visits at Baseline, Week 6, Week 12, and Week 24.
Compensation
Not stated in the trial record.
Follow-up
The primary endpoint, social communication symptoms, will be measured at Week 24, which is the end of treatment.

AI-generated from the public study record. Only the study team can confirm whether you're eligible — confirm details with them before making decisions.

NCT04060030

Treatment of Social and Language Deficits With Leucovorin for Young Children With Autism

Recruiting
PHASE2Ages 30–60InterventionalTreatment
Southwest Autism Research & Resource Center
~80 participants
Updated 2026-04-27 on ClinicalTrials.gov
What's tested:Levoleucovorin CalciumPlacebo

At a glance

Recruiting sites
1 of 2 listed sites are recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Evaluate the change in social communication symptoms
Measured over Baseline, Week 6, Week 12, Week 24
Autism Spectrum Disorder
Language Disorders
2 sites across 2 states
Arizona1
New York1
  • Richard E Frye, MD, PhD · PRINCIPAL_INVESTIGATOR · Rossignol Medical Center, Phoenix AZ

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  • Evaluate the change in social communication symptomsBaseline, Week 6, Week 12, Week 24

    Aberrant Behavior Checklist-2, Social Withdrawal Subscale. The ABC is a 58-item parent-reported measure with ratings in the following domains: irritability, social withdrawal, stereotypic behavior, hyperactivity, and inappropriate speech. Each item is rated from 0 (Not a Problem) to 3 (Severe Problem). The raw score will be reported. The total raw score is the sum of the domain raw scores. A higher raw score in any of the domains indicates more severe problems in that domain; a higher total raw score indicates more severity of stereotypical autism symptoms overall.