Study of BGB-11417 for Myeloid Malignancies

This study is testing a new drug called BGB-11417, both alone and with another drug called azacitidine, for people with certain blood cancers. These include acute myeloid leukemia (AML), myelodysplastic syndromes (MDS), or myelodysplastic/myeloproliferative neoplasm (MDS/MPN). The main goals are to see how safe BGB-11417 is, what side effects it might cause, and to find the best dose. Researchers will also look at how well the treatment works, for example, if it leads to a complete remission (when signs of cancer disappear). You might be able to join if you are 18 or older, have one of these conditions, and meet other health requirements. The study plans to enroll about 260 participants, but its current status is unclear.

Study design
This is an interventional study, meaning participants will receive specific treatments. It aims to enroll 260 participants, but the phase is not specified.
What's involved
You would take BGB-11417 by mouth for a set number of days in a 28-day cycle. Some participants might also receive azacitidine by injection or posaconazole by mouth.
Compensation
Not stated in the trial record.
Follow-up
Researchers will monitor participants for side effects for approximately 24 months. They will also check for complete remission in some groups around 24 months.

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NCT04771130

A Study of BGB-11417 in Participants With Myeloid Malignancies

Recruiting
PHASE1Ages 18+InterventionalTreatment
BeOne Medicines
~260 participants
Updated 2026-07-13 on ClinicalTrials.gov
What's tested:BGB-11417AzacitidinePosaconazole

At a glance

Recruiting sites
43 of 46 listed sites are recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Part 1 And 2: Number Of Participants Experiencing Dose-limiting Toxicities (DLTs)
Measured over Cycle 1 (Up to 28 days for non-hematologic DLTs and up to 42 days for hematologic DLTs)
+8 more outcomes measured
Acute Myeloid Leukemia
Myelodysplastic Syndromes
Myelodysplastic/Myeloproliferative Neoplasm
46 sites across 26 states
Victoria4
Spain4
New South Wales3
Western Australia3
Guangdong3
France3
Italy3
Germany2
  • Study Director · STUDY_DIRECTOR · BeOne Medicines

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Do you actually qualify for this trial?

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Eligibility criteria

Inclusion

AML, nonacute promyelocytic leukemia
MDS
MDS/MPN 2. Eastern Cooperative Oncology Group performance status of 0 to 2. 3. Adequate organ function defined as:
Creatinine clearance ≥ 50 milliliters/minute (mL/min) (or between 30 and 49 mL/min in unfit AML cohort)
Adequate liver function 4. Life expectancy of \> 12 weeks. 5. Ability to comply with the requirements of the study.
  • Part 1 And 2: Number Of Participants Experiencing Dose-limiting Toxicities (DLTs)Cycle 1 (Up to 28 days for non-hematologic DLTs and up to 42 days for hematologic DLTs)
  • Part 1 And 2: Number Of Participants Experiencing Treatment-emergent Adverse Events (TEAEs)Approximately 24 months
  • Part 3 AML Cohort: Complete Remission (CR) Plus CR With Partial Hematologic Recovery (CRh) RateApproximately 24 months

    CR plus CRh will be defined as the percentage of participants whose best overall response (BOR) is CR plus CRh. BOR will be defined as the best response recorded from the first dose of study drug until data cut or the initiation of new anticancer treatment.

  • Part 3 MDS Cohort: Modified Overall Response (mOR) RateApproximately 24 months

    The mOR will be defined as the percentage of participants whose BOR is achieving CR, marrow complete remission (mCR), or partial remission (PR) at any time point during the study for myelodysplastic/myeloproliferative neoplasm (MDS/MPN).

  • Part 3 AML Cohort (DDI Sub-cohort): Area Under Plasma Concentration-time Curve (AUC) from time 0 to the last quantifiable timepoint (t) (AUC0-t) Of BGB-11417 When Administered Alone and when Co-administered With PosaconazoleCycle 2 Day 12 and Cycle 2 Day 20 (predose and 1, 2, 4, 6, 8, and 24 hours postdose)
  • Part 3 AML Cohort (DDI Sub-cohort): Maximum Observed Plasma Concentration (Cmax) Of BGB-11417 When Administered Alone and When Co-administered With PosaconazoleCycle 2 Day 12 and Cycle 2 Day 20 (predose and 1, 2, 4, 6, 8, and 24 hours postdose)
  • Part 3 AML Cohort (DDI Sub-cohort): Area Under Plasma Concentration-time Curve (AUC) from time 0 to infinity (AUC0-infinity) Of BGB-11417 When Administered Alone and When Co-administered With PosaconazoleCycle 2 Day 12 and Cycle 2 Day 20 (predose and 1, , 4, 6, 8, and 24 hours postdose)
  • Part 3 AML and MDS Cohorts (Treated with Monotherapy): Number Of Participants Experiencing DLTsCycle 2
  • Part 3 AML and MDS Cohorts (Treated with Monotherapy): Number of Participants Experiencing TEAEsApproximately 24 months