NCT05868499

Rollover Study From EXG-US-01

Enrolling by Invitation
PHASE1Ages 18+InterventionalSupportive care
Elixirgen Therapeutics, Inc.
~12 participants
Updated 2024-07-12 on ClinicalTrials.gov
What's tested:EXG34217

At a glance

Recruiting sites
0 of 1 listed site is recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Number of participants with adverse events -Safety by Incidence of Treatment-Emergent
Measured over Change from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72
+4 more outcomes measured
Telomere Biology Disorders With Bone Marrow Failure
1 sites across 1 states
Ohio1
  • Kasiani Myers, MD · PRINCIPAL_INVESTIGATOR · Cincinnati Children Hospital Medical Center

This trial hasn't published a contact. View it on ClinicalTrials.gov

  • Number of participants with adverse events -Safety by Incidence of Treatment-EmergentChange from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72

    Number of participants with treatment-related adverse events as assessed by CTCAE v4.03. Incidence and nature of adverse events, vital signs, weight.

  • umber of participants with a change in in physical examinationChange from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72

    Physical examination changes General appearance ,Head, eyes, ears, nose, and throat, Respiratory, Cardiovascular, Musculoskeletal, Abdomen, Neurologic, Extremities, Dermatologic, Lymphatic)

  • Number of participants with a change in Electrocardiography (ECG)Change from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72

    ECG (standard digital 12-lead in singlicate)

  • Number of participants with a change in clinical laboratory evaluationsChange from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72

    Changes in clinical laboratory evaluations (Hematology, Blood chemistry, Coagulation, and Urinalysis)

  • Number of participants with a change of ImmunogenicityChange from Baseline Systolic Blood Pressure at Month 18, 24,30,36,42,48,60 and 72

    Change in Antibody against virus vector and transgene