A Study of Ranolazine for ALS

This study is looking at ranolazine, a medication, to see if it is safe and helps with muscle cramps, daily function, and quality of life for people with Amyotrophic Lateral Sclerosis (ALS). You might be able to join if you are 18 or older, have a diagnosis of ALS, and your breathing assessment (forced vital capacity or FVC) is at least 50%. You also need to be able to swallow pills. The study will compare two different doses of ranolazine (500mg or 1000mg, both taken twice daily) to a placebo (an inactive pill that looks like the study drug). Researchers will be looking at how often side effects occur, how well people tolerate the treatment, and how often muscle cramps happen over about 28 weeks. The current recruitment status is unclear.

Study design
This is a multi-center, double-blind, placebo-controlled study involving about 72 adults with ALS. Participants will be randomly assigned to receive either ranolazine or a placebo.
What's involved
You would take ranolazine or placebo twice daily for approximately 28 weeks. You would also attend a minimum of 5 in-person research visits and 4 remote research visits.
Compensation
Not stated in the trial record.
Follow-up
The primary outcomes, such as side effect frequency and muscle cramp frequency, will be measured for up to 28 weeks.

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NCT06527222

A Study of Ranolazine in ALS

Recruiting
PHASE2Ages 18+InterventionalTreatment
Swathy Chandrashekhar, MBBS
~72 participants
Updated 2026-06-08 on ClinicalTrials.gov
What's tested:RanolazinePlacebo

At a glance

Recruiting sites
6 of 6 listed sites are recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Frequency of Treatment-Emergent Adverse Events
Measured over Up to 28 weeks
+10 more outcomes measured
Amyotrophic Lateral Sclerosis

NCT06527222

Where you'd take part

This study runs at 6 sites. They're the same protocol — you choose where, and that choice sets who your contact draft is addressed to.

  • Mayo Clinic Florida

    Jacksonville, Floridastudy coordinator listed

    Recruiting

  • The Ohio State University

    Columbus, Ohiostudy coordinator listed

    Recruiting

  • University of California, San Francisco

    San Francisco, Californiastudy coordinator listed

    Recruiting

  • University of Kansas Medical Center

    Fairway, Kansasstudy coordinator listed

    Recruiting

  • University of Kansas Medical Center: Wichita

    Wichita, Kansasstudy coordinator listed

    Recruiting

  • University of Missouri Health Care

    Columbia, Missouristudy coordinator listed

    Recruiting

Sites open and close at different times, so the status above is per site — it can differ from the study's overall status.

  • Jeffrey Statland, MD · PRINCIPAL_INVESTIGATOR · University of Kansas Medical Center

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Eligibility criteria

Inclusion

18 years or older
Diagnosed with clinically definite, possible, probably, or lab-supported probable ALS per revised El Escorial criteria
Breathing assessment called forced vital capacity (FVC) greater than or equal to 50%.
Able to swallow pills at the start of the study and expected to for the length of the study.
If on ALS modifying medications must be on a stable dose at least 30 days.
Experiencing 4 or more cramps per week during a 2-week screening period.

Exclusion

Disease duration \< 5 years
Tracheostomy invasive ventilation, or noninvasive ventilation of more than 12 hours/day
Pregnant or lactating, adults unable to consent, and prisoners
Taking ranolazine or investigational drug or has received an investigational drug within 30 days (or 5 half-lives for drugs, whichever is longer) prior to screening
Medically uncontrolled comorbidities (heart, liver, kidney disease)
Baseline QTc interval prolongation \>450 ms for men/ \>470 ms for women, history of long QT syndrome, or medications which prolong the QT interval
Participation in an experimental drug trial less than 30 days before screening
Patients have to be on a stable dosage of any medications used to treat muscle cramps for ≥30 days or have been off these medications ≥30 days prior to randomization.
  • Frequency of Treatment-Emergent Adverse EventsUp to 28 weeks

    Patient report and medical records will be used to document adverse events and severe adverse events. Adverse events and severe adverse events will be assessed by the investigator and reported as needed for safety.

  • Tolerability of treatment assignmentUp to 28 weeks

    Tolerability will be measured by percentage of patients who complete the treatment assignment. Dose limiting toxicities will be determined by individual with an adverse event necessitating stopping.

  • Muscle cramp frequencyUp to 28 weeks

    Muscle cramp frequency will be measured numerically with a reporting period of 7 days. Changes will be compared from baseline to week 28 utilizing a modified Qualitative, Patient-Centered Assessment of Muscle Cramp Impact and Severity questionnaire.

  • Muscle cramp severityUp to 28 weeks

    Muscle cramp severity will be measured by a score of 1-10 (1 being a very mild muscle cramp and 10 being the most severe cramp you ever experienced). Changes will be compared from baseline to week 28 utilizing a modified Qualitative, Patient-Centered Assessment of Muscle Cramp Impact and Severity questionnaire.

  • Muscle cramps impact on quality of lifeUp to 28 weeks

    Effect of muscle cramps on quality of life will be measured with three patient reported yes or no questions (Yes indicating an impact on quality of life or no indicating no impact on quality of life). Changes will be compared from baseline to week 28 utilizing a modified Qualitative, Patient-Centered Assessment of Muscle Cramp Impact and Severity questionnaire

  • Safety Lab Cystatin CUp to 28 weeks

    Patient safety measured with lab value Cystatin C in mg/L.

  • Safety Lab Estimated Glomerular Filtration Rate (eGFR)Up to 28 weeks

    Patient safety measured with lab value eGFR in mL/min/1.73.

  • Safety Lab Alanine Transaminase (ALT)Up to 28 weeks

    Patient safety measured with lab value ALT in IU/L.

  • Safety Lab Aspartate Transferase (AST)Up to 28 weeks

    Patient safety measured with lab value AST in IU/L.

  • Safety Lab Alkaline Phosphatase (ALP)Up to 28 weeks

    Patient safety measured with lab value ALP in IU/L.

  • Safety Lab Total BilirubinUp to 28 weeks

    Patient safety measured with lab value total bilirubin in mg/dL.