Phase 1/2 Study of SB-007 for Stargardt Disease

This study is testing a new treatment called SB-007, given as a shot under the retina (subretinal injection), for people with Stargardt Disease (STGD1). Stargardt Disease is an inherited eye condition that can cause vision loss. The main goals of this study are to see how safe SB-007 is, how well people tolerate it, and if it shows any early signs of improving vision. You may be able to join if you are between 12 and 65 years old. The study aims to enroll about 57 people and will follow them for 96 weeks after a single treatment. The current recruitment status is unclear.

Study design
This is a Phase 1/2 study, meaning it's an early-stage trial. It will include about 57 participants to evaluate the safety and initial effectiveness of SB-007.
What's involved
Participants will receive a single subretinal injection of SB-007 and will be followed for 96 weeks after treatment.
Compensation
Not stated in the trial record.
Follow-up
Participants will be followed for 96 weeks after receiving the treatment to monitor safety.

AI-generated from the public study record. Only the study team can confirm whether you're eligible — confirm details with them before making decisions.

NCT06942572

A Phase 1/2, First-in-Human Dose Escalation/Expansion Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of a Subretinal Injection of SB-007 in Subjects With Stargardt Disease (STGD1)

Recruiting
PHASE1Ages 12–65InterventionalTreatment
Splice Bio
~57 participants
Updated 2025-04-29 on ClinicalTrials.gov
What's tested:SB-007

At a glance

Recruiting sites
5 of 5 listed sites are recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Safety Measures
Measured over 96 weeks
Stargardt Disease
Stargardt Macular Degeneration
Stargardt Macular Dystrophy
5 sites across 5 states
Colorado1
Florida1
Massachusetts1
Oregon1
Texas1

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  • Safety Measures96 weeks

    Safety and tolerability assessed by incidence and/or clinically significant changes in ocular and non-ocular AEs