ADI-PEG 20, Temozolomide, and Radiation for Newly Diagnosed High-Grade Glioma

This study is testing a combination of treatments for newly diagnosed high-grade glioma (a type of brain tumor) in children, adolescents, and young adults. The treatments include ADI-PEG 20 (arginine deiminase pegylated), Temozolomide (TMZ), and standard radiation therapy (RT). Researchers want to see how safe this combination is and how well it works to stop the tumor from growing. You could be eligible if you are between 3 and 39 years old and have a newly diagnosed high-grade glioma, including specific types like glioblastoma or diffuse midline glioma. The study will look at side effects and how long patients live without their disease getting worse.

Study design
This is an open-label study, meaning everyone knows which treatments are being given. It aims to enroll 97 participants and will evaluate the safety and effectiveness of the treatment combination.
What's involved
Not specified in the trial record.
Compensation
Not stated in the trial record.
Follow-up
Participants will be followed for up to 104 weeks to monitor side effects, and for up to 12 months to assess how long they live without the disease progressing.

AI-generated from the public study record. Only the study team can confirm whether you're eligible — confirm details with them before making decisions.

NCT07389278

Combination ADI-PEG 20, TMZ, and RT for Treatment of Newly Diagnosed High-grade Glioma (HGG)

Not Yet Recruiting
PHASE1Ages 3–39InterventionalTreatment
Sabine Mueller, MD, PhD
~97 participants
Updated 2026-02-05 on ClinicalTrials.gov
What's tested:ADI-PEG 20 (Arginine deiminase pegylated)Temozolomide (TMZ)Standard of Care Radiation Therapy (RT)

At a glance

Recruiting sites
0 of 1 listed site is recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
Proportion of participants with Treatment-emergent Adverse Events (TrAE) (Phase 1)
Measured over Up to 104 weeks
+3 more outcomes measured
Glioblastoma
High-Grade Glioma (WHO III-IV)
High-grade Glioma
Diffuse Midline Glioma, H3 K27M-Mutant
Diffuse Hemispheric Glioma, H3G34 Mutant
1 sites across 1 states
California1
  • Sabine Mueller, MD, PhD · PRINCIPAL_INVESTIGATOR · University of California, San Francisco
  • Tom Davidson, MD · STUDY_CHAIR · Children's Hospital Los Angeles

Opens a ready-to-send draft in your own email app — review before sending.

Do you actually qualify for this trial?

Add a private profile and we'll compare every criterion below against your situation — and tell you which ones are met, uncertain, or excluding.

Check eligibility for this trial ~2 min · HIPAA-protected · delete anytime
Eligibility criteria

Inclusion

Cohort 1: Newly diagnosed non-pontine, non-spinal cord HGG histone-wildtype.
Cohort 2: Newly diagnosed non-pontine, non-spinal cord H3K27 altered diffuse midline glioma (DMG).
Cohort 3: Newly diagnosed non-pontine, non-spinal cord H3G34 mutant diffuse hemispheric glioma (DHG). 2. Prior surgery: must have undergone maximal safe resection. For patients with DMG of the pons, biopsy is sufficient. 3. Prior Therapy: Participants must NOT have received ANY prior therapy (except surgery) before enrollment on study. 4. Tumor Tissue Requirement: Participants must have sufficient tumor tissue (5-10 unstained formalin-fixed paraffin-embedded (FFPE) slides or a tumor block) for study enrollment. 5. Age:
Cohort 1: 3 to 25 years of age.
Cohorts 2 \& 3: 3 to 39 years of age. 6. Performance Score: Karnofsky \>= 50 for participants \> 16 years of age and Lansky \>= 50 for participants \<=16 years of age. Participants who are unable to walk because of paralysis, but who are up in a wheelchair, will be considered ambulatory for the purpose of assessing the performance score. 7. Corticosteroids: Participants who are receiving dexamethasone must be on a stable or decreasing dose for at least 1 week prior to registration. 8. Organ Function Requirements:
  • Proportion of participants with Treatment-emergent Adverse Events (TrAE) (Phase 1)Up to 104 weeks

    Proportion of participants in Phase 1 with treatment-emergent adverse events as graded by National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE version 5.0) will be reported.

  • Progression-Free Survival (PFS) for HGG histone-WT (Phase 2, Cohort 1)Up to 12 months

    PFS for participants in Phase 2, Cohort 1 is defined as the median number of days participants remained progression free at 12 months. Participants without a documented tumor progression or death will be censored on the date of their last evaluable tumor assessment. Participants without a documented tumor progression or death before initiation of another anti-tumor therapy will be censored on the date of their last evaluable tumor assessment prior to or on the date of the new anti-tumor therapy. PFS estimates will be obtained from the Kaplan-Meier curve. An appropriate variance term that accounts for censoring Greenwood's formula) will be used to construct the 95% confidence intervals.

  • Progression-Free Survival (PFS) for H3K27 altered diffuse midline glioma (DMG) (Phase 2, Cohort 2)Up to 12 months

    PFS for participants in Phase 2, Cohort 2 is defined as the median number of days participants remained progression free at 12 months. Participants without a documented tumor progression or death will be censored on the date of their last evaluable tumor assessment. Participants without a documented tumor progression or death before initiation of another anti-tumor therapy will be censored on the date of their last evaluable tumor assessment prior to or on the date of the new anti-tumor therapy. PFS estimates will be obtained from the Kaplan-Meier curve. An appropriate variance term that accounts for censoring Greenwood's formula) will be used to construct the 95% confidence intervals.

  • Progression-Free Survival (PFS) for H3G34 mutant diffuse hemispheric glioma (DHG) (Phase 2, Cohort 3)Up to 10 months

    PFS for participants in Phase 2, Cohort 3 is defined as the median number of days participants remained progression free at 10 months. Participants without a documented tumor progression or death will be censored on the date of their last evaluable tumor assessment. Participants without a documented tumor progression or death before initiation of another anti-tumor therapy will be censored on the date of their last evaluable tumor assessment prior to or on the date of the new anti-tumor therapy. PFS estimates will be obtained from the Kaplan-Meier curve. An appropriate variance term that accounts for censoring Greenwood's formula) will be used to construct the 95% confidence intervals.