CTX310 for Refractory Dyslipidemias

This study is testing a new treatment called CTX310 for people with dyslipidemias (high cholesterol and triglycerides) that haven't improved with other treatments. CTX310 uses a special technology called CRISPR to target a gene involved in how your body handles fats. The main goal of this study is to see how safe CTX310 is for you, and if you can tolerate it, over a period of up to 12 months after receiving the treatment. You might be able to join if you are between 18 and 75 years old and have specific levels of high triglycerides or cholesterol. This study is currently enrolling participants.

Study design
This is a Phase 1, single-arm, open-label study, meaning all 90 participants will receive CTX310, and both you and the study team will know which treatment you are getting.
What's involved
You will receive CTX310 through an intravenous (IV) infusion. The study will monitor your safety for up to 12 months after this infusion.
Compensation
Not stated in the trial record.
Follow-up
Your safety will be monitored for up to 12 months after receiving the CTX310 infusion.

AI-generated from the public study record. Only the study team can confirm whether you're eligible — confirm details with them before making decisions.

NCT07491172

A Safety and Tolerability Trial Evaluating CTX310 in Participants With Refractory Dyslipidemias

Recruiting
PHASE1Ages 18–75InterventionalTreatment
CRISPR Therapeutics AG
~90 participants
Updated 2026-07-23 on ClinicalTrials.gov
What's tested:CTX310

At a glance

Recruiting sites
13 of 19 listed sites are recruiting right now
RecruitingSuspended, closed, or not yet open
What they're measuring
To evaluate the safety of CTX310 in adult subjects with dyslipidemias that are refractory to available treatments
Measured over From CTX310 infusion up to 12 months
Cardiovascular
Metabolic Disease
Dyslipidemias
Lipid Disorder
Hypertriglyceridemia
Heterozygous Familial Hypercholesterolemia (HeFH)
Homozygous Familial Hypercholesterolemia (HoFH)
Severe Hypertriglyceridemia (sHTG)
Mixed Hyperlipemia
Hypercholesterolaemia
19 sites across 8 states
Australia5
Florida4
United Kingdom3
North Carolina2
New Zealand2
New York1
Ohio1
Oregon1

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  • To evaluate the safety of CTX310 in adult subjects with dyslipidemias that are refractory to available treatmentsFrom CTX310 infusion up to 12 months

    Incidence of dose-limiting toxicities and frequency of adverse events