Gaucher Disease clinical trials
12 active trials name this condition. Describe your situation to see which ones look like a fit.
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- Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease
- The GBA Multimodal Study in Parkinson's Disease
- Gaucher Disease Outcome Survey (GOS)
- A Long-term Follow-up Study of Gaucher Disease
- International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
- FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
- Registry of Patients Diagnosed With Lysosomal Storage Diseases
- Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- Longitudinal Study of Neurodegenerative Disorders
- Genetic Studies of Lysosomal Storage Disorders
- ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
- Drug Discovery for Parkinson's With Mutations in the GBA Gene
Guides for people searching for a trial
- Why people get turned down — and what to do nextWhat eligibility criteria are for, what keeps people out, and where to go when the first door closes.
- How your biomarkers decide which trials you qualify forEGFR, HER2, BRAF, PD-L1 and the rest — what they are and why they increasingly gate access.
- How to search for a trial without losing your mindWhere to look, what to gather first, and how to read what you find.
- What Phase 1, 2 and 3 actually mean for youWhat each phase is testing, and how to weigh an early-phase trial against a later one.
- 10 questions to ask before you say yesTreatment, time, cost, safety and your rights. Worth bringing to a screening visit.
- You matched with a trial. What happens now?Phone screens, the screening visit, informed consent, and day one.
Showing active trials that list “Gaucher Disease” as a condition. Eligibility shown on each trial is an estimate — the trial's study team makes the final decision.